Skip to content

About GM1 Gangliosidosis
- - - About
  - - Treatments and Research
      - Advancements and Research
      - Gene Therapy
    - If Your Loved One Has GM1
How to Help
- - - Subscribe to Our YouTube Channel
What We Do
- - - Guide Families
    - Drive Progress and Research

Research

2016 Cyclodextrin GM1 Pilot Study

Byraj October 15, 2018January 13, 2024

GM1 Cyclodextrin Pilot Study Initiated

This experiment was ceased due to lack of efficacy.

Post navigation

2015-2017 Auburn/UMass Research Intravenous AAV9 Gene Therapy

2017 UC Davis Lentiviral Gene Therapy Research

501(c)(3) EIN: #47-3154419

PO Box 6890, Albany
CA 94706, USA
1-510-306-2460

Cure GM1 does not prescribe medications or treatments. This information is being shared for educational purposes and discussion with your doctors.

Useful Links

Privacy Policy
Terms and Conditions
Contact Us
Subscribe to Newsletter
Refund Policy

Your Help Matters

© 2024 CureGM1. Maintained by RRethink.

About GM1 Gangliosidosis
How to Help
What We Do