Cure GM1 Presents to the FDA for the Inaugural Meeting of the Rare Disease Innovation Hub
This meeting was organized by the FDA and the Reagan Udall Foundation at the White…
Lingxi’s Story
Lingxi’s GM1 Story, as told by her father Her GM1 Story ” We have been…
Hampus, Julia, And Isabella’s Story
Hampus, Julia, and Isabella’s Story Their GM1 Stories “It is heartbreaking not knowing what tomorrow…
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Sanofi Press Release: AMETHIST Trial Discontinued
We regret to inform you that in Sanofi’s quarterly press release issued today that the…
The March 2024 Cure GM1 Catalyst
2024 Cure GM1 Virtual Conference We are excited to start planning our annual conference for…
2023 Cure GM1 Impact Report – Impact In 2023 And Beyond
Our summary of impact in 2023 is now available to read. After some time reflecting, everyone…
Iris’ Story from Her Brother’s Perspective
As told by Iris’ brother. How has GM1 gangliosidosis affected your life? GM1 Gangliosidosis is…
Marley’s Story
How did you feel when your child received a diagnosis of GM1? Early on we…
Jessica’s Story
How did you feel when you received a diagnosis of GM1? When I got my…