Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021
Cure GM1 is pleased to share the tremendous news that both Passage Bio and Lysogene have received regulatory approvals…
Cas’ Story
From Cas’ Mother: Cas was a beautiful, happy boy. He had beautiful eyes and hair…
Sofia and Stephanie
Sofia, developed up to 1 year and 8 months as a normal child, regression began…
Nastya’s Story
Nastya’s Story Until the age of one year old, Nastya grew and developed like an…
Darian’s Story
DONATE We are living a parents worst nightmare. Our sweet son Darian, was recently diagnosed…
Elena’s Story
Elena was diagnosed at age 23 and is from Russia. She is the rare of…
Robert’s Story
Robert Ernest Mitchell Messer suffered from infantile GM1 and passed away on July 30,2019
Stella and Finya
Beautiful Stella and Finya passed away within one day of one another. Finya passed…
Tyson’s Story
Our dear little Tyson was born on September 15, 1989 and lived a short 16…
James’ Story
From James’ Mother: James was diagnosed with GM1 Gangliosidosis Type 2 Juvenile on November 7,…