Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021
Cure GM1 is pleased to share the tremendous news that both Passage Bio and Lysogene have received regulatory approvals…
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Clara’s Story
Please watch Clara’s family’s video: This is a wonderful article about Clara and her family’s…
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Cas’ Story
From Cas’ Mother: Cas was a beautiful, happy boy. He had beautiful eyes and hair…
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Sofia and Stephanie
Sofia, developed up to 1 year and 8 months as a normal child, regression began…
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Nastya’s Story
Nastya’s Story Until the age of one year old, Nastya grew and developed like an…
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Darian’s Story
DONATE We are living a parents worst nightmare. Our sweet son Darian, was recently diagnosed…
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Conference Speakers
Cure GM1 Conference Speakers Release Thank you for applying to be a speaker. First Name[text*…
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Elena’s Story
Elena was diagnosed at age 23 and is from Russia. She is the rare of…
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Lindsay’s Story
Lindsay is kind and humorous. Her favorite movie is Tombstone. She loves theme parks and…
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Robert’s Story
Robert Ernest Mitchell Messer suffered from infantile GM1 and passed away on July 30,2019