Research
Cure GM1 recently granted funds towards the development of a lentiviral gene therapy approach using…
GM1 Cyclodextrin Pilot Study Initiated This experiment was ceased due to lack of efficacy.
Cure GM1 funded pre-clinical studies, IND-enabling studies, and the Pre-IND briefing document for intravenous AAV9…
This clinical study was being conducted at University of Minnesota where the ketogenic diet was…
Stories
Althea was born on 23rd September 2016, a beautiful 6lb 8oz baby girl. Thea was…
A beautiful baby boy born February 16, 2012 Paxton is our first and only child,…
#AWin4Kate Kate was born May 17, 2011, a healthy and happy baby. We always thought…
A special boy that fought to the end Joe was born 4 weeks early by…
Una Bellisima Bambina Paola is a beautiful child born on June 29, 2013. She was…
