Luigi’s story
Hi friends, my name is Luigi. I’m Italian, and I’ll be 3 in October. Unfortunately…
The April 2023 Cure GM1 Catalyst
Take Action Take Action for GM1 Day Now is the time to buy GM1 Day…
2022 Cure GM1 Impact Report – Impact in 2022 and Beyond
Our summary of impact in 2022 is now available to read. After some time reflecting,…
The March 2023 Cure GM1 Catalyst
Amazing Advocacy this Rare Disease Day Our community really showed up to participate in Rare…
Diego’s Story
Diego was born on June 29, 2021 in Imola, a small town in Italy. We…
The Voice of the Patient Report from the GM1 Gangliosidosis Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD)
You can now download and read the touching and impactful summary of input from GM1…
About the GM1 Gangliosidosis Externally-Led Patient-Focused Drug Development (EL-PFDD) Meeting with FDA
The GM1 Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD) was held on Friday, October 14 as…
The February 2023 Cure GM1 Catalyst
Rare Disease Day is on February 28, 2023. Leading up to the day, there are…
Rare Disease Day Photo Contest Entry Form
The 2023 Cure GM1 RDD Photo Contest Calling all photographers! Photo submissions for the 2023…
Cure GM1 Caregiver Preferences Study has been published
Our Caregiver Preferences study, The caregivers’ assessments of symptom impact and most important symptoms to…