Sofia, developed up to 1 year and 8 months as a normal child, regression began at 1 year and 9 months. At 2 years and 2 months she was diagnosed with gangliosidosis. At the moment, Sofia knows how to eat on her own, has support on her legs, fixes her gaze and monitors objects, turns from side to side. Sofia has a younger sister, Stephanie, who is now 1 year and 6 months old with the same diagnosis. We look forward to the treatment of our daughters.

Stephanie is developing like an ordinary child, at the moment there is no loss of skills, in August 2020 she was 1 year and 6 months old, she was diagnosed with GM1 gangliosidosis at birth. Stephanie has an older sister, Sofia, 4 years and 5 months old with the same diagnosis. We look forward to the treatment of our daughters.